[ad_1] The FDA approval of BioMarin’s gene therapy for hemophilia is a major win, but patient uptake could be slow. [ad_2] Source link
Tag: Genetic Disorders
New Gene Therapy Could Face Uphill Battle
[ad_1] The potential FDA approval of BioMarin’s gene therapy for hemophilia A would be a major win, but patient uptake could be slow. [ad_2] Source link
Drug Prices Reach New High—in the Millions
[ad_1] Several new drugs, most of them gene therapies, promise one-time treatments, but their price tags will test the health-insurance system. [ad_2] Source link
Opinion | Biden’s Race Against a Cure
[ad_1] Updated Nov. 13, 2023 7:27 pm ET The Food and Drug Administration may soon approve two gene therapies with the potential to cure more than 100,000 Americans with debilitating…